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Aqneursa (levacetylleucine)

The FDA approved Aqneursa (levacetylleucine) on September 24, 2024 to treat Niemann-Pick disease type C.

Brand name: Aqneursa
Generic name: levacetylleucine
FDA approval date: September 24, 2024
Approved use (FDA wording): To treat Niemann-Pick disease type C
Category on this site: Rare & genetic

Official sources

FDA novel drug approvals list
FDA announcement

Facts only. This site lists what the FDA has approved and what the FDA says each drug is approved for, quoted or closely paraphrased from FDA and openFDA records. It gives no medical advice, no dosing, and no comparisons, and it says nothing about whether a drug is right for anyone. Talk to a licensed clinician about any medication. Records can lag or contain errors; the FDA's own pages are authoritative.